| ALNY | Alnylam Pharmaceuticals |
| BBIO | BridgeBio Pharma |
| BEAM | Beam Therapeutics |
| BMRN | BioMarin Pharmaceutical |
| CRSP | CRISPR Therapeutics |
| IONS | Ionis Pharmaceuticals |
| NTLA | Intellia Therapeutics |
| PTCT | PTC Therapeutics |
| RARE | Ultragenyx Pharmaceutical |
| SRPT | Sarepta Therapeutics |