| ADRX | ADARx Pharmaceuticals |
| RNAZ | TransCode Therapeutics |
| RNA | Atrium Therapeutics |
| ARCT | Arcturus Therapeutics |
| IONS | Ionis Pharmaceuticals |
| PRQR | ProQR Therapeutics |
| ARWR | Arrowhead Pharmaceuticals |
| SRPT | Sarepta Therapeutics |
| BNTC | Benitec Biopharma |
| WVE | Wave Life Sciences |