| STOK | Stoke Therapeutics |
| ALNY | Alnylam Pharmaceuticals |
| ARCT | Arcturus Therapeutics |
| IONS | Ionis Pharmaceuticals |
| ARWR | Arrowhead Pharmaceuticals |
| PRQR | ProQR Therapeutics |
| SRPT | Sarepta Therapeutics |
| NTLA | Intellia Therapeutics |
| SLN | Silence Therapeutics |
| BNTC | Benitec Biopharma |